Leveraging Adeno-Associated Viruses (AAVs) in therapeutic approaches for monogenic neurological diseases
Supplied by PerkinElmer on Wednesday, 07 September, 2022
Within the field of neurological diseases, there is great interest in looking at rare diseases of monogenic origin with the hope of developing disease-modifying gene therapies, as opposed to treatments for symptom management. Therefore, using relatively tunable systems like recombinant AAVs, scientists are also exploring in vivo gene delivery in parallel to ex vivo.
Learn about key strategies and innovations in this space that are enabling advanced gene therapy.
Related White Papers
Next-gen weight-data integration: cloud, IT and control system connectivity
Discover the latest innovations that can...
8 ways to ensure data integrity in life science
Along with background information and links to all relevant regulations and guidance documents,...
Advantages of Wavelength Scanning in Fluorescence and Absorbance Assays
EnVision® Multilabel Plate Reader, widely used in biological assay studies across the field...
