Leveraging Adeno-Associated Viruses (AAVs) in therapeutic approaches for monogenic neurological diseases
Supplied by PerkinElmer on Wednesday, 07 September, 2022
Within the field of neurological diseases, there is great interest in looking at rare diseases of monogenic origin with the hope of developing disease-modifying gene therapies, as opposed to treatments for symptom management. Therefore, using relatively tunable systems like recombinant AAVs, scientists are also exploring in vivo gene delivery in parallel to ex vivo.
Learn about key strategies and innovations in this space that are enabling advanced gene therapy.
Related White Papers
Protective solutions for glove allergies
Wearing glove products can cause adverse skin reactions, ranging from irritant contact...
Minimise the measurement uncertainty in your lab
Learn about the importance of measurement uncertainty in the manufacturing and use of certified...
Digital innovation drives smarter, faster biologics development
[Case study] From bottleneck to breakthroughs: a...
